MBE RNA editing based RNA seq
1. Experimental Purpose
Scientific Question : What are the direct RNA targets and precise binding sites of RNA-binding protein X in living cells?
Design Rationale : Fusion of RNA-binding protein (RBP) to an RNA editing enzyme (APOBEC) creates a chimeric protein that marks RNA binding sites with C-to-U conversions, detectable by RNA-seq without crosslinking artifacts
Follow-up Studies : Motif analysis of binding sites, functional validation of key targets, structural studies of RBP-RNA interactions, comparison with other RBP mapping techniques (CLIP-seq)
2. Model System
Primary System : Human cell line relevant to RBP function (e.g., neuronal cells for neuron-specific RBPs, cancer cells for cancer-relevant RBPs)
Rationale : Cell lines provide controlled expression of the RBP-APOBEC fusion, high RNA yield, and consistent experimental conditions
Alternatives :
Primary cells (pros: physiological relevance; cons: transfection challenges, variability)
Mouse models with inducible RBP-APOBEC (pros: in vivo context; cons: complex, expensive)
In vitro transcribed RNAs (pros: defined sequences; cons: lacks cellular context)
Ethical Considerations : Cell line authentication, appropriate biosafety practices, responsible use of genetic modification tools
3. Measurement Approach
Techniques :
Doxycycline-inducible expression of RBP-APOBEC fusion
RNA extraction with DNase treatment
Strand-specific RNA-seq with high depth
C-to-U editing site identification
Technical Replicates : Duplicate RNA-seq libraries
Potential Biases :
Expression level variations of RBP-APOBEC (use inducible system with titrated expression)
Off-target editing (include catalytically inactive APOBEC control)
RNA degradation artifacts (optimize RNA extraction protocol)
Sequence context preferences of APOBEC (account for in computational analysis)
4. Group Setting
Experimental Groups :
Test: Cells expressing RBP-APOBEC fusion
Control 1: Cells expressing catalytically inactive APOBEC fusion (deaminase mutant)
Control 2: Cells expressing APOBEC only (no RBP)
Control 3: Cells expressing GFP-APOBEC (non-specific RNA binding)
Control 4: Uninduced cells (baseline editing)
Controlled Variables : Induction time, expression level, RNA quality, sequencing depth
Biological Replicates : 3-4 independent inductions and RNA preparations
Modified Design : Include time-course of induction to capture kinetics of editing, or RBP mutants with altered RNA-binding specificity
5. Data Analysis & Presentation
Data Processing :
Read alignment to reference genome
C-to-U conversion identification
Background filtering using controls
Peak calling to identify significant binding sites
Motif discovery in binding regions
Statistical Analysis :
Statistical significance of editing sites above background
Enrichment analysis for RNA types and cellular compartments
Correlation with RBP expression levels
Comparison with known binding motifs or CLIP-seq data
Data Presentation :
Genome browser tracks showing editing sites
Metagene plots of binding distribution across transcript regions
Motif logos for identified binding sequences
Venn diagrams comparing targets with other datasets
Functional enrichment maps of target RNAs
Validation Methods :
RT-qPCR validation of editing at selected sites
CLIP-seq or RIP-seq for orthogonal validation
Functional assays for key targets (e.g., minigene reporters)
Mutagenesis of binding sites to confirm direct interaction
RNA structure probing to assess structural context of binding
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